Reimbursement status, access delays and prices of orphan drugs in France: a population-stratified analysis of indications approved between 2021 and 2024

Orphanet Journal of Rare Diseases · Published 2026-08-05 · DOI 10.1186/s13023-026-04533-w

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Authors (3)

Izzat Sultan, Pascal Paubel, Albane Degrassat-Théas

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Publication details

Year

2026

Citation

Sultan, I., Paubel, P., Degrassat-Théas, A. (2026). Reimbursement status, access delays and prices of orphan drugs in France: a population-stratified analysis of indications approved between 2021 and 2024. Orphanet Journal of Rare Diseases. https://doi.org/10.1186/s13023-026-04533-w

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