Paediatric palliative approach in the era of disease modifying therapies in spinal muscular atrophy — a comprehensive landscape of French specialist physicians’ perspectives

Orphanet Journal of Rare Diseases · Published 2026-08-05 · DOI 10.1186/s13023-026-04481-5

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Authors (5)

Marie-Liesse Guenée, Claire Pilet, Hélène Martinez, Véronique Christophe, Matthias Schell

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Publication details

Year

2026

Citation

Guenée, M., Pilet, C., Martinez, H., et al. (2026). Paediatric palliative approach in the era of disease modifying therapies in spinal muscular atrophy — a comprehensive landscape of French specialist physicians’ perspectives. Orphanet Journal of Rare Diseases. https://doi.org/10.1186/s13023-026-04481-5

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