Bone- and muscle-targeted adeno-associated viral vectors enable tissue-selective vitamin D receptor knockdown in mice

GENE THERAPY · Published 2026-07-29 · DOI 10.1038/s41434-026-00636-y

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Authors (9)

Alexandra K. O’Donohue, Julian Chu, Nicholas Norris, Hsien-Yin Kao, Josephine Yu, Lucinda R. Lee, Dirk Grimm, Jenny E. Gunton, Aaron Schindeler

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Publication details

Year

2026

Citation

O’Donohue, A., Chu, J., Norris, N., et al. (2026). Bone- and muscle-targeted adeno-associated viral vectors enable tissue-selective vitamin D receptor knockdown in mice. GENE THERAPY. https://doi.org/10.1038/s41434-026-00636-y

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