Research map: Cholesterol nose-to-brain delivery as a possible therapeutic strategy in Huntington’s disease
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Papers in this map
Exon 1 of the HD Gene with an Expanded CAG Repeat Is Sufficient to Cause a Progressive Neurological Phenotype in Transgenic Mice
· Laura Mangiarini · 1996 · 3117 citations · Cited by this paper
Cholesterol restores corticostriatal synaptic connectivity in Huntington’s disease through BDNF/TrkB signalling, supporting a role for cholesterol pathways implicated by human genetic modifier studies
· Allegra Lenci · 2026 · Cites this paper
Application of the Allen Human Brain Atlas in Alzheimer’s disease and Parkinson’s disease
· 2026 · Related
Aggregation of Huntingtin in Neuronal Intranuclear Inclusions and Dystrophic Neurites in Brain
· Marian DiFiglia · 1997 · 2933 citations · Cited by this paper
Nanotechnological and in vivo characterization of a new generation of brain-permeable nanoparticles for brain-targeted cholesterol delivery in Huntington’s disease
· Giulia Birolini · 2026 · Cites this paper
Age-dependent removal of Atg9-containing vesicle accumulations in motoneuron disease models by physical exercise
· 2025 · Related
Thematic review series: Brain Lipids. Cholesterol metabolism in the central nervous system during early development and in the mature animal
· John M. Dietschy · 2004 · 1095 citations · Cited by this paper
Reduced synaptic vesicle protein 2A in extracellular vesicles and brains of Alzheimer’s disease: associations with Aβ, tau, synaptic proteins and APOE ε4
· 2025 · Related
Linking lipids to Alzheimer's disease: cholesterol and beyond
· Gilbert Di Paolo · 2011 · 1000 citations · Cited by this paper
Targeting the glymphatic system: Aβ accumulation and phototherapy strategies across different stages of Alzheimer’s disease
· 2025 · Related
Lipid Rafts in the Maintenance of Synapses, Dendritic Spines, and Surface AMPA Receptor Stability
· Heike Hering · 2003 · 602 citations · Cited by this paper
Attenuating α-synuclein pathology in mice with in situ engineered astrocytes
· 2025 · Related
Direct nose to brain drug delivery via integrated nerve pathways bypassing the blood–brain barrier: an excellent platform for brain targeting
· Chandrakantsing Vijaysing Pardeshi · 2013 · 479 citations · Cited by this paper
Stratification of brain-derived extracellular vesicles of Alzheimer’s disease patients indicates a unique proteomic content and a higher seeding capacity of small extracellular vesicles
· 2025 · Related
Crossing the barrier: oxysterols as cholesterol transporters and metabolic modulators in the brain
· Ingemar Björkhem · 2006 · 384 citations · Cited by this paper
LRRK2 G2019S mutation contributes to mitochondrial transfer dysfunction in a Drp1-STX17-dependent manner
· 2025 · Related
Neurofilament light protein in blood as a potential biomarker of neurodegeneration in Huntington's disease: a retrospective cohort analysis
· Lauren M. Byrne · 2017 · 372 citations · Cited by this paper
Proximity labeling in neuroscience: decoding molecular landscapes for precision neurology
· 2026 · Related
Cholesterol 24-Hydroxylase: An Enzyme of Cholesterol Turnover in the Brain
· David W. Russell · 2009 · 337 citations · Cited by this paper
Microbiota and Alzheimer’s disease: mechanistic insights from a multi-organ perspective
· 2026 · Related
Role of cholesterol in synapse formation and function
· Frank W. Pfrieger · 2003 · 330 citations · Cited by this paper
Lysophagy protects against ANXA11 amyloid fibril toxicity and propagation in FTLD
· 2026 · Related
Intranasal delivery of nanostructured lipid carriers, solid lipid nanoparticles and nanoemulsions: A current overview of in vivo studies
· Cláudia Pina Costa · 2021 · 303 citations · Cited by this paper
Dysfunction of the Cholesterol Biosynthetic Pathway in Huntington's Disease
· Marta Valenza · 2005 · 302 citations · Cited by this paper
Nose-to-brain delivery of lipid-based nanosystems for epileptic seizures and anxiety crisis
· Cláudia Pina Costa · 2019 · 208 citations · Cited by this paper
CYP46A1, the rate-limiting enzyme for cholesterol degradation, is neuroprotective in Huntington’s disease
· Lydie Boussicault · 2016 · 197 citations · Cited by this paper
Ontogenesis and regulation of cholesterol metabolism in the central nervous system of the mouse
· Gang Quan · 2003 · 178 citations · Cited by this paper
Altered cholesterol and fatty acid metabolism in Huntington disease
· Robert Block · 2009 · 156 citations · Cited by this paper
Revisiting nanoparticle technology for blood–brain barrier transport: Unfolding at the endothelial gate improves the fate of transferrin receptor-targeted liposomes
· Kasper Bendix Johnsen · 2015 · 131 citations · Cited by this paper
Cholesterol biosynthesis pathway is disturbed in YAC128 mice and is modulated by huntingtin mutation
· Marta Valenza · 2007 · 130 citations · Cited by this paper
Progressive dysfunction of the cholesterol biosynthesis pathway in the R6/2 mouse model of Huntington’s disease
· Marta Valenza · 2007 · 127 citations · Cited by this paper
CYP46A1 gene therapy deciphers the role of brain cholesterol metabolism in Huntington’s disease
· Radhia Kacher · 2019 · 118 citations · Cited by this paper
Mutant huntingtin and neurofilament light have distinct longitudinal dynamics in Huntington’s disease
· Filipe Brogueira Rodrigues · 2020 · 114 citations · Cited by this paper
Cholesterol‐loaded nanoparticles ameliorate synaptic and cognitive function in Huntington's disease mice
· Marta Valenza · 2015 · 113 citations · Cited by this paper
Oxysterol research: a brief review
· William James Griffiths · 2019 · 107 citations · Cited by this paper
Cerebrospinal Fluid Biomarkers for Huntington’s Disease
· Lauren M. Byrne · 2016 · 81 citations · Cited by this paper
Cholesterol Hydroxylating Cytochrome P450 46A1: From Mechanisms of Action to Clinical Applications
· Irina A. Pikuleva · 2021 · 80 citations · Cited by this paper
Visualizing Cholesterol in the Brain by On-Tissue Derivatization and Quantitative Mass Spectrometry Imaging
· Roberto Angelini · 2021 · 74 citations · Cited by this paper
Altered Cholesterol Homeostasis in Huntington’s Disease
· Radhia Kacher · 2022 · 67 citations · Cited by this paper
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