Research map: First bone marrow transplantation for mucopolysaccharidosis type I in Vietnam: a case report

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  27. Long-term outcomes of systemic therapies for Hurler syndrome: an international multicenter comparison · Julie B. Eisengart · 2018 · 75 citations · Cited by this paper
  28. Enzyme Replacement is Associated with Better Cognitive Outcomes after Transplant in Hurler Syndrome · Julie B. Eisengart · 2012 · 74 citations · Cited by this paper
  29. Enzyme replacement therapy prior to haematopoietic stem cell transplantation in Mucopolysaccharidosis Type I: 10year combined experience of 2 centres · Arunabha Ghosh · 2016 · 61 citations · Cited by this paper
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  34. Mortality after hematopoietic stem cell transplantation for severe mucopolysaccharidosis type I: the 30‐year University of Minnesota experience · Nathan J. Rodgers · 2017 · 41 citations · Cited by this paper
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  36. Intrathecal Enzyme Replacement Therapy for Mucopolysaccharidosis I: Translating Success in Animal Models to Patients · Patricia Dickson · 2011 · 39 citations · Cited by this paper
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