Clinical Development of Therapies for Charcot–Marie–Tooth Disease: Recommendations for Trial Design, Endpoints, and Regulatory Pathways

Journal of the Peripheral Nervous System · Published 2026-08-04 · DOI 10.1111/jns.70146

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Authors (14)

Charles K. Abrams, Sue Bruhn, Joshua Burns, Rebekah Fleming, Katherine Forsey, Vera Fridman, David N. Herrmann, Brian Lin, Susan McCune, Allison Moore, Susan Ruediger, Michael Shy, Shannon Strom, ToPIC:CMT Steering Committee

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Publication details

Year

2026

Citation

Abrams, C., Bruhn, S., Burns, J., et al. (2026). Clinical Development of Therapies for Charcot–Marie–Tooth Disease: Recommendations for Trial Design, Endpoints, and Regulatory Pathways. Journal of the Peripheral Nervous System. https://doi.org/10.1111/jns.70146

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