Safety, Tolerability, and Efficacy of a Prophylactic Sirolimus Protocol for Patients Receiving Delandistrogene Moxeparvovec-Rokl Gene Therapy

HUMAN GENE THERAPY · Published 2026-08-05 · DOI 10.1177/10430342261472609

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Authors (9)

Zahraa Siddiqui, Serena Neumann, Daniel Guillen, Ruchee Patel, Rachel Cox, W. Bryan Burnette, Rachel Harris, Saeed Mohammad, Jonathan H. Soslow

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Year

2026

Citation

Siddiqui, Z., Neumann, S., Guillen, D., et al. (2026). Safety, Tolerability, and Efficacy of a Prophylactic Sirolimus Protocol for Patients Receiving Delandistrogene Moxeparvovec-Rokl Gene Therapy. HUMAN GENE THERAPY. https://doi.org/10.1177/10430342261472609

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