Regulatory Alignment on Surrogate Endpoints for Slowly Progressive Ultra-Rare Neurological Diseases: Bridging the Gap Between Biomarker Science and Global Regulatory Acceptance

Therapeutic Innovation and Regulatory Science · Published 2026-07-29 · DOI 10.1007/s43441-026-01026-7

Authors (2)

Shihshuan Fang, Shenghan Chen

Abstract

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Publication details

Year

2026

Citation

Fang, S., Chen, S. (2026). Regulatory Alignment on Surrogate Endpoints for Slowly Progressive Ultra-Rare Neurological Diseases: Bridging the Gap Between Biomarker Science and Global Regulatory Acceptance. Therapeutic Innovation and Regulatory Science. https://doi.org/10.1007/s43441-026-01026-7

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