Kebilidi (eladocagene exuparvovec-tneq) for adults and children with aromatic L-amino acid decarboxylase (AADC) deficiency: A therapeutics bulletin of the American College of Medical Genetics and Genomics (ACMG)

Julie M. Porter; Andrés Morales Corado; Kuntal Sen; Sarah H. Elsea

doi:10.1016/j.gimo.2025.103471

Kebilidi (eladocagene exuparvovec-tneq) for adults and children with aromatic L-amino acid decarboxylase (AADC) deficiency: A therapeutics bulletin of the American College of Medical Genetics and Genomics (ACMG)

Genetics in Medicine Open · Published 2026-06-01 · DOI 10.1016/j.gimo.2025.103471

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Julie M. Porter, Andrés Morales Corado, Kuntal Sen, Sarah H. Elsea

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Year: 2026

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Porter, J., Corado, A., Sen, K., et al. (2026). Kebilidi (eladocagene exuparvovec-tneq) for adults and children with aromatic L-amino acid decarboxylase (AADC) deficiency: A therapeutics bulletin of the American College of Medical Genetics and Genomics (ACMG). Genetics in Medicine Open. https://doi.org/10.1016/j.gimo.2025.103471

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Kebilidi (eladocagene exuparvovec-tneq) for adults and children with aromatic L-amino acid decarboxylase (AADC) deficiency: A therapeutics bulletin of the American College of Medical Genetics and Genomics (ACMG)

Authors (4)

Abstract

Publication details

Citation

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