Accelerating access to gene therapy: Lessons from commercial implementation in sickle cell disease and transfusion-dependent thalassemia

Journal of Sickle Cell Disease · Published 2026-06-01 · DOI 10.1093/jscdis/yoag020.006

Free full text

Authors (11)

Anjuiika Chawla, Melissa Kinney, Bevin Noone, Theresa Chera, Kenneth Christianson, Joanne Lager, Brian Riley, Tom Klima, Vinod Prasad, Ravi Singh, Melanie Weinsten

Abstract

PubPorta does not have an abstract for this article yet.

Read the article at the publisher →

Publication details

Year

2026

Citation

Chawla, A., Kinney, M., Noone, B., et al. (2026). Accelerating access to gene therapy: Lessons from commercial implementation in sickle cell disease and transfusion-dependent thalassemia. Journal of Sickle Cell Disease. https://doi.org/10.1093/jscdis/yoag020.006

Related articles

• Transdermal Curcumin Gel (VAS-101 Drug Candidate) Improves the Microcirculation and Tissue Oxygenation in a Rat Model of Sickle Cell Vaso-Occlusive Episode · Journal of Sickle Cell Disease · 2026 · Same journal
• Altered Sensory-Pain Transitions in Sickle Cell Disease Reflect Central Sensitization · Journal of Sickle Cell Disease · 2026 · Same journal
• Long Term Anticoagulation for Venous Thromboembolism in Sickle Cell Disease: A Systematic Review (1995–December 2025) · Journal of Sickle Cell Disease · 2026 · Same journal
• Public Health Awareness of Sickle Cell Anemia: A Qualitative Descriptive Study among Educated Young Adults in India · Journal of Sickle Cell Disease · 2026 · Same journal
• Using Electronic-Medical Records to Facilitate Transition From Pediatric to Adult Hematology for Sickle Cell Disease · Journal of Sickle Cell Disease · 2026 · Same journal
• Warrior Intelligence: A Community-Led Navigation Infrastructure for Real-Time Sickle Cell Crisis Data and Clinical Blind Spot Detection · Journal of Sickle Cell Disease · 2026 · Same journal
• Patient-Specific Modeling Reveals Stroke-Related Cerebral Hemodynamic Changes in Adults With Sickle Cell Disease · Journal of Sickle Cell Disease · 2026 · Same journal
• Dietary Antioxidant Intake and Associations with Self-Reported Pain Among Adults Living with Sickle Cell Disease in the U.S · Journal of Sickle Cell Disease · 2026 · Same journal
• From Sidelines to Systems: An Interprofessional Model for Supporting Athletes with Sickle Cell Disease · Journal of Sickle Cell Disease · 2026 · Same journal
• Association between Newborn Sickle Cell Disease and Low Birth Weight Among Full-term Births: A Population-Based Study in the State of Virginia (2014- 2023) · Journal of Sickle Cell Disease · 2026 · Same journal