Haematopoetic stem and progenitor cell gene therapy for metachromatic leukodystrophy: Mission possible!

European Journal of Paediatric Neurology · Published 2026-08-01 · DOI 10.1016/j.ejpn.2026.07.010

Authors (2)

Yılmaz Yıldız, Göknur Haliloğlu

Abstract

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Publication details

Year

2026

Citation

Yıldız, Y., Haliloğlu, G. (2026). Haematopoetic stem and progenitor cell gene therapy for metachromatic leukodystrophy: Mission possible!. European Journal of Paediatric Neurology. https://doi.org/10.1016/j.ejpn.2026.07.010

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