Cross-Correction in HSC Gene Therapy for Metachromatic Leukodystrophy

New England Journal of Medicine · Published 2026-07-29 · DOI 10.1056/nejmc2505002

Authors (17)

Vasco Meneghini, Valeria Calbi, Filippo Casalini, Elisabeth Mangiameli, Francesco Morena, Marco Piccoli, Ilaria Laface, Ilaria Rossomanno, Francesca Ornaghi, Andrea Ghiroldi, Paola M.V. Rancoita, Francesca Fumagalli, Sabata Martino, Luigi Anastasia, Luigi Naldini, Alessandro Aiuti, Angela Gritti

Abstract

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Publication details

Year
2026

Citation

Meneghini, V., Calbi, V., Casalini, F., et al. (2026). Cross-Correction in HSC Gene Therapy for Metachromatic Leukodystrophy. New England Journal of Medicine. https://doi.org/10.1056/nejmc2505002

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