New England Journal of Medicine · Published 2026-07-29 · DOI 10.1056/nejmc2505002
Vasco Meneghini, Valeria Calbi, Filippo Casalini, Elisabeth Mangiameli, Francesco Morena, Marco Piccoli, Ilaria Laface, Ilaria Rossomanno, Francesca Ornaghi, Andrea Ghiroldi, Paola M.V. Rancoita, Francesca Fumagalli, Sabata Martino, Luigi Anastasia, Luigi Naldini, Alessandro Aiuti, Angela Gritti
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Meneghini, V., Calbi, V., Casalini, F., et al. (2026). Cross-Correction in HSC Gene Therapy for Metachromatic Leukodystrophy. New England Journal of Medicine. https://doi.org/10.1056/nejmc2505002