JAMA Cardiology · Published 2026-06-17 · DOI 10.1001/jamacardio.2026.1699
Ronald G. Crystal, Jonathan W. Weinsaft, Stephen M. Kaminsky, Anthony Caragiulo, Niamh Savage, Aarti Patel, Ralitza H. Gavrilova, Susan L. Perlman, Madeline Galbraith, Udhay Kahlon, Udhay Krishnan, Robert J. Kaner, Abraham Sanders, Mary Vo, Harini Sarva, Andrea Yoo, Dolan Sondhi, Bishnu P. De, Jason G. Mezey, Gregory Aubert, Aashir Khan, Nithya Selvan, Narinder Bhalla, Eric Adler, Theresa Zesiewicz
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Crystal, R., Weinsaft, J., Kaminsky, S., et al. (2026). AAVrh.10hFXN Gene Therapy for the Cardiomyopathy of Friedreich Ataxia. JAMA Cardiology. https://doi.org/10.1001/jamacardio.2026.1699