Neonatal expression of human FMRP isoform corrects cortical deficits and improves behavior in a mouse model of fragile X syndrome

MOLECULAR THERAPY NUCLEIC ACIDS · Published 2026-06-12 · DOI 10.1016/j.omtn.2026.102981

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Authors (13)

Anna O. Norman, Courtney Scaramella, Dominik Biezonski, Ralph D. Hector, Alexandra Varallo, Aarushi Sahni, Nadia Farooq, Suzanne R. Burstein, Juliana Benito, Khaleel A. Razak, Jim Selfridge, Stuart Cobb, Iryna M. Ethell

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Year

2026

Citation

Norman, A., Scaramella, C., Biezonski, D., et al. (2026). Neonatal expression of human FMRP isoform corrects cortical deficits and improves behavior in a mouse model of fragile X syndrome. MOLECULAR THERAPY NUCLEIC ACIDS. https://doi.org/10.1016/j.omtn.2026.102981

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