Long-term reversal of Duchenne muscular dystrophy via circular arRNA-guided exon skipping in monkeys and humans

Cell · Published 2026-06-10 · DOI 10.1016/j.cell.2026.05.030

Authors (34)

Wenting Guo, Huixian Tang, Zongyi Yi, Ting Zhang, Pengfei Yuan, Cuijin Wang, Shuaiwei Ren, Xiwen Chang, Jiwu Ren, Wei Tang, Wenjie Sun, Jie Liu, Ying Yu, Zhiwei Lu, Hongyan Shen, Zexuan Yi, Yanxia Zhao, Gangbin Tang, Junyuan Han, Wenzhi Zhang, Haoyue Liu, Xueqing Sun, Yongjian Zhang, Cui Zhang, Yuming Wu, Ling Yang, Feng Han, Yichao Xu, Liang Qu, Xinyan Sun, Jiwen Wang, Weizhi Ji, Yongchang Chen, Wensheng Wei

Abstract

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Publication details

Year
2026

Citation

Guo, W., Tang, H., Yi, Z., et al. (2026). Long-term reversal of Duchenne muscular dystrophy via circular arRNA-guided exon skipping in monkeys and humans. Cell. https://doi.org/10.1016/j.cell.2026.05.030

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